Patent Portfolio
Therapeutic agent for x-linked sideroblastic anemia
| Ref. No. | AJ255 |
|---|---|
| Appl. No. （filing date） |
PCT/JP2021/042347（2021/11/11） |
| Pub. No. （Pub. date） |
WO2022/145144（2022/7/7） |
| Priority claim No. （Priority date） |
JP2020-218557（2020/12/28) |
| Inventor | YOSHIDA, Yoshinori, et al. |
| Assignee | Kyoto University |
| Title of Invention | Therapeutic agent for x-linked sideroblastic anemia |
| Abstract | The present invention provides a pharmaceutical composition for treating X-linked sideroblastic anemia, the composition comprising a demethylating agent, in particular, 5-azacitidine or a derivative thereof; and normal erythroid cells that are differentiated and induced from iPS cells derived from a patient with X-linked sideroblastic anemia in the presence of a demethylating agent. |
| Information (External link) |
https://www.j-platpat.inpit.go.jp/c1800/PU/WO-A-2022-145144/D88C1BCE7C9AD7605ACBC5EEC5646EE7B15B334F6523DA49DAACC101246EAB98/50/en |